Любовь Ширижик (Старший редактор отдела «Силовые структуры»)
onlinelibrary.wiley.com
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The CuRe trial is now enrolling up to 35 patients in its Phase 1/2a study. Children will be followed through age 6 to evaluate long-term safety and early signs of improved movement, bladder and bowel function.
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